canonical disease area

Neuromuscular Disorders
Intelligence

Neuromuscular Disorders intelligence: 51 indexed trials, 19 recruiting studies, 44 sponsors across 41 countries.

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51Indexed trials
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19Recruiting
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44Sponsors
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41Countries

Leading sponsors

Hoffmann-La Roche40 recruiting
Catalyst Pharmaceuticals, Inc.21 recruiting
Biogen21 recruiting
argenx22 recruiting
Italfarmaco21 recruiting
BioMarin Pharmaceutical10 recruiting
Beth Israel Deaconess Medical Center10 recruiting
Ann & Robert H Lurie Children's Hospital of Chicago10 recruiting
Charitable Foundation Children with Spinal Muscular Atrophy10 recruiting
Catholic University of the Sacred Heart10 recruiting
Copenhagen University Hospital, Rigshospitalet10 recruiting
Barts & The London NHS Trust10 recruiting

Geographic activity

United States31trials
United Kingdom20trials
Italy19trials
Germany17trials
France16trials
Spain16trials
Belgium15trials
Canada14trials
Japan12trials
Australia10trials
Poland10trials
China9trials

Leading interventions

Risdiplam2trials
Rituximab2trials
Ataluren1trials
Cladribine Low Dose1trials
Direct current stimulation of cervical spinal cord1trials
Drisapersen1trials
Efgartigimod PH20 SC1trials
Efgartigimod IV1trials
Exondys 511trials
Flavocoxid1trials
Givinostat1trials
Cladribine High Dose1trials

Methodology note

This entity is derived from structured ClinicalTrials.gov conditions and/or MeSH normalization. Counts reflect the current NeuroRisk indexed corpus and are not guaranteed exhaustive global totals.