12Indexed trials
mesh condition
Rare Diseases
Intelligence
Rare Diseases intelligence: 12 indexed trials, 5 recruiting studies, 11 sponsors across 17 countries.
5Recruiting
11Sponsors
17Countries
Leading sponsors
National Center for Research Resources (NCRR)20 recruiting
Friedreich's Ataxia Research Alliance11 recruiting
Istituto Auxologico Italiano11 recruiting
Johns Hopkins University10 recruiting
National Institute of Mental Health (NIMH)10 recruiting
Novartis Pharmaceuticals10 recruiting
Sanford Health11 recruiting
UMC Utrecht11 recruiting
University Hospital, Strasbourg, France10 recruiting
Connecta Therapeutics, S.L.11 recruiting
University of California, Los Angeles10 recruiting
Geographic activity
United States5trials
Australia3trials
France3trials
Italy3trials
Netherlands3trials
Spain3trials
New Zealand2trials
Germany2trials
Austria2trials
United Kingdom2trials
Canada2trials
Brazil1trials
Leading interventions
CTH1201trials
CTH120 placebo hard capsules1trials
Cannabidiol (CBD) oral solution1trials
Glucose1trials
Individualized in home parent training1trials
PTC5181trials
Questionnaires, clinical scales and instrumental tests1trials
albendazole1trials
cosyntropin1trials
dexamethasone1trials
intensive one-on-one behavioral treatment1trials
metyrapone1trials
Methodology note
This entity is derived from structured ClinicalTrials.gov conditions and/or MeSH normalization. Counts reflect the current NeuroRisk indexed corpus and are not guaranteed exhaustive global totals.